first demonstration that the prime editing approach can efficiently correct in cellular model the frequenct Familial Dysautonomia-causing c.2204+6T>C splicing mutation
Prime editing of the common Familial Dysautonomia-causing c.2204+6T>C splicing mutation
Laura PerettoPrimo
;Mirko PinottiPenultimo
;Dario Balestra
Ultimo
2026
Abstract
first demonstration that the prime editing approach can efficiently correct in cellular model the frequenct Familial Dysautonomia-causing c.2204+6T>C splicing mutationFile in questo prodotto:
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